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News & Trends - Pharmaceuticals

TGA approves Vertex’s cystic fibrosis therapy 6-11 year olds

Health Industry Hub | November 3, 2022 |

Pharma News: Vertex announced that the Australian Therapeutic Goods Administration (TGA) has approved the use of Trikafta (elexacaftor/tezacaftor/ivacaftor and ivacaftor) for children with cystic fibrosis (CF) ages 6-11 years who have at least one F508del mutation in the CF transmembrane conductance regulator (CFTR) gene, the most common CF-causing mutation worldwide.

Cystic Fibrosis begins at birth and leads to cumulative health decline over time, and premature death. In paediatric patients, there is evidence of early structural lung damage, even prior to the emergence of symptoms, including those of a respiratory nature.
“This approval follows the recent PBS listing for those ages 12 years and older and demonstrates our continued commitment to broaden access to younger Australians with CF,” said Sabrina Barbic, Senior Country Manager, Australia and New Zealand, Vertex Pharmaceuticals.

“We now look forward to the outcome of the Pharmaceutical Benefits Advisory Committee (PBAC) meeting in November, at which Trikafta will be considered for reimbursement for this younger age group. We will continue to work tirelessly alongside the CF community and other stakeholders in an effort to bring Trikafta to all Australian patients who can benefit.”

Trikafta was approved by the TGA based on the results of data from a 24-week Phase 3 study, which evaluated the safety and efficacy of Trikafta in children ages 6-11 years with at least one F508del mutation.


News & Trends - Pharmaceuticals

Lilly's drug cuts diabetes risk by 94%, so why is it still not on the PBS?

Lilly’s drug cuts diabetes risk by 94%, so why is it still not on the PBS?

Health Industry Hub | November 14, 2024 |

On World Diabetes Day (14 November), new data reveals that three years of treatment with a GIP/GLP-1 receptor agonist significantly […]

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News & Trends - Biotechnology

Depaz Oration to celebrate an 'enduring' legacy in the biotech sector

Depaz Oration to celebrate an ‘enduring’ legacy in the biotech sector

Health Industry Hub | November 14, 2024 |

AusBiotech announced the establishment of the Depaz Oration, an annual keynote event that will debut at the AusBiotech Conference in […]

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News & Trends - Pharmaceuticals

Government calls for public input on genomic-led cancer care

Government calls for public input on genomic-led cancer care

Health Industry Hub | November 14, 2024 |

The Australian Government has launched a public consultation on a draft policy framework aimed at enhancing genomics-informed cancer care nationwide. […]

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News & Trends - MedTech & Diagnostics

Can the patient voice reduce low-value care? Australia’s first large-scale hospital initiative seeks answers

Can the patient voice reduce low-value care? Australia’s first large-scale hospital initiative seeks answers

Health Industry Hub | November 14, 2024 |

In an Australian-first, a not-for-profit private health insurer will ask hospital patients to rate not only their clinical care but […]

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